Q12 of 57 Page 85

Gene therapy is an attempt to correct a genetic defect by providing a normal gene into the individual. By this the normal function can be restored. An alternate method would be to provide the gene product (protein/enzyme) known as enzyme replacement therapy, which would also restore the function. Which in your opinion is a better option? Give reason for your answer.

- Enzyme replacement therapy is not a permanent method to cure the disease as it is needed to be given at regular intervals to the patient.


- Due to the potential to completely cure the genetic defect, gene therapy is considered to be a better option.


If, gene replacement is done during embryonic condition it could be a permanent cure


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